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  • Research Updates,
• 4/24/26

Updates on successful fragile X knockout mouse research program

April 24, 2026

Previous

Excited about start of Mirum trial as we learn soon about the Shionogi/Tetra results

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Updated Findings about Fragile X Gene Methylation

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Cincinnati Children’s Hospital Medical Center
3333 Burnet Avenue
Cincinnati, OH 45229-3026

513-803-1150

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fragilex@cchmc.org